New transplant method aims to tame dangerous side effects for rare blood disease patients
NCT ID NCT04965597
Summary
This study tested a new combination of drugs given before a bone marrow or blood stem cell transplant. The goal was to see if this new 'conditioning' regimen could help patients with rare bone marrow failure diseases have fewer and less severe complications after their transplant. The trial involved 40 patients under age 50 with specific genetic blood disorders. Researchers measured success by looking at survival without major side effects like graft-versus-host disease one year after the procedure.
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Contacts and locations
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Locations
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Boston Children's Hospital
Boston, Massachusetts, 02115, United States
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Children's Healthcare of Atlanta
Atlanta, Georgia, 30329, United States
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Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Children's Hospital Los Angeles
Los Angeles, California, 90027, United States
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Cincinnati Children's Hospital
Cincinnati, Ohio, 45229, United States
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Cohen Children's Hospital of NY
Queens, New York, 11040, United States
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Duke University Medical Center
Durham, North Carolina, 27705, United States
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Fred Hutch/University of Washington Cancer Consortium
Seattle, Washington, 98109, United States
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Johns Hopkins University
Baltimore, Maryland, 21231, United States
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MD Anderson Cancer Center
Houston, Texas, 77030, United States
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Medical College of Wisconsin/Children's Hospital of Wisconsin
Milwaukee, Wisconsin, 53226, United States
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Memorial Sloan Kettering Cancer Center
New York, New York, 10065, United States
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Oregon Health & Science University
Portland, Oregon, 97239, United States
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Primary Children's/University of Utah
Salt Lake City, Utah, 84113, United States
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Rady Children's Hospital/UCSD
San Diego, California, 92123, United States
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Roswell Park Comprehensive Cancer Center
Buffalo, New York, 14203, United States
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St. Louis Children's Hospital
St Louis, Missouri, 63110, United States
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Texas Children's Hospital
Houston, Texas, 77030, United States
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University of California San Francisco
San Francisco, California, 94143, United States
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University of Michigan Medical Center
Ann Arbor, Michigan, 48109, United States
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University of Minnesota
Minneapolis, Minnesota, 55455, United States
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Vanderbilt University Medical Center
Nashville, Tennessee, 37232, United States
Conditions
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