First pill for genetic lung & liver disease enters human testing
NCT ID NCT06738017
Summary
This is a very early study to check if a new oral drug called BMN 349 is safe for people with Alpha-1 Antitrypsin Deficiency, a genetic condition that can damage the lungs and liver. A small group of 12 adults with specific genetic types of the disease will take a single dose of either the drug or a placebo (a dummy pill). Researchers will closely monitor participants for any side effects and measure how the drug moves through the body.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Medpace Clinical Pharmacology Unit
RECRUITINGCincinnati, Ohio, 45227, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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NHS Lothian
RECRUITINGEdinburgh, UK, United Kingdom
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Nottingham University Hospitals
NOT_YET_RECRUITINGNottingham, UK, United Kingdom
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Royal Free London NHS Foundation Trust
RECRUITINGLondon, UK, United Kingdom
Contact Email: •••••@•••••
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Saint Louis University
RECRUITINGSt Louis, Missouri, 63110, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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The Medical University of South Carolina
RECRUITINGCharleston, South Carolina, 29425, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University Hospital Southampton NHS Foundation Trust
RECRUITINGSouthampton, UK, United Kingdom
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of California, San Diego
RECRUITINGSan Diego, California, 92037, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
Explore the condition pages connected to this study.