One-Shot gene therapy tested in boys with devastating muscle disease
NCT ID NCT07058662
Summary
This early-stage study is testing a new, one-time gene therapy called BBM-D101 for boys with Duchenne Muscular Dystrophy (DMD). The main goal is to see if the treatment is safe and well-tolerated. Researchers will also check if it helps improve muscle strength and function over a year, with follow-up for up to five years.
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Contacts and locations
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Study contacts
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Contact
Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Peking Union Medical College Hospital
RECRUITINGBeijing, Beijing Municipality, 100730, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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