New drug trial offers hope for debilitating mast cell disease symptoms

NCT ID NCT03731260

Summary

This study is testing whether the drug avapritinib can better control symptoms in adults with indolent systemic mastocytosis whose symptoms are not well-managed by current standard treatments. It's a Phase 2 trial where some participants receive the drug and others receive a placebo, along with standard supportive care, to compare effectiveness and safety. The main goal is to see if avapritinib significantly reduces the total burden of disease symptoms compared to placebo.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • A.O. OO.RR. S.Giovanni di Dio e Ruggi d'Aragona, University of Salerno

    Salerno, 84131, Italy

  • A.O.U di Bologna - IRCCS, Istituto di Ematologia Lorenzo e Ariosto Seragnoli, Ematologia

    Bologna, 40138, Italy

  • Akademiska sjukhuset, Hematologmottagningen/101A

    Uppsala, 751 85, Sweden

  • Azienda Ospedaliera Universitaria Integrata di Verona

    Verona, 37126, Italy

  • Brigham & Women's Hospital

    Boston, Massachusetts, 02115, United States

  • CHU Toulouse Larrey, CEREMAST, Service de Dermatologie et Allergologie cutanée

    Toulouse, 31059, France

  • Charité Universitätsmedizin Berlin

    Berlin, 10117, Germany

  • Clatterbridge Cancer Centre NHS Foundation Trust

    Metropolitan Borough of Wirral, CH63 4JY, United Kingdom

  • Dana Farber Cancer Institute

    Boston, Massachusetts, 02215, United States

  • Duke University Health System (DUHS)

    Durham, North Carolina, 27710, United States

  • Erasmus Medical Center

    Rotterdam, 3015 GD, Netherlands

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Poloclinico, UOC Ematologia

    Milan, 20122, Italy

  • Guy's and St Thomas' NHS Foundation Trust - Guy's Hospital

    London, SE1 9RT, United Kingdom

  • H. Lee Moffitt Cancer Center

    Tampa, Florida, 33612, United States

  • Herbert Irving Comprehensive Cancer Center

    New York, New York, 10032, United States

  • Hospital Universitari Vall d'Hebron

    Barcelona, 08035, Spain

  • Huntsman Cancer Institute

    Salt Lake City, Utah, 84112, United States

  • Hôpital Pitié-Salpêtrière, Service de Dermatologie

    Paris, 75013, France

  • Hôpital de la Timone, Service de dermatologie

    Marseille, 13385, France

  • Karolinska University Hospital, Hematologimottagningen R51

    Stockholm, 141 86, Sweden

  • Klinikum rechts der Isar, Technische Universität München

    Munich, 80802, Germany

  • Mayo Clinic

    Rochester, Minnesota, 55905, United States

  • Mayo Clinic Florida

    Jacksonville, Florida, 32224, United States

  • Mayo Clinic Hospital

    Phoenix, Arizona, 85054, United States

  • Michigan Medicine, University of Michigan

    Ann Arbor, Michigan, 48106, United States

  • NHS Greater Glasgow and Clyde, Beatson West of Scotland Cancer Centre

    Glasgow, G12 OXL, United Kingdom

  • Odense Universitetshospital, ORCA/Allergicentret, Hudafdeling I og Allergicenter

    Odense, DK-5000, Denmark

  • Oslo Universitetssykehus, Rikshospitalet, Department of Hematology

    Oslo, 0372, Norway

  • Rush University Medical Center

    Chicago, Illinois, 60612, United States

  • St. Michael's Hospital

    Toronto, Ontario, M5B 1W8, Canada

  • Stanford Cancer Institute

    Stanford, California, 94305, United States

  • Tom Baker Cancer Centre

    Calgary, Alberta, T2N 4N2, Canada

  • Uniklinik RWTH Aachen

    Aachen, 52074, Germany

  • University Clinic Hamburg Eppendorf, University Cancer Center Hamburg (UCCH)

    Hamburg, 20246, Germany

  • University Hospital Antwerp

    Edegem, 2650, Belgium

  • University Hospital Basel

    Basel, 4031, Switzerland

  • University Hospitals Cleveland Medical Center

    Cleveland, Ohio, 44106, United States

  • University Medical Center Groningen (UMCG)

    Groningen, 9713 GZ, Netherlands

  • University of Alabama at Birmingham

    Birmingham, Alabama, 35294, United States

  • University of Alberta Hospital

    Edmonton, Alberta, T6G 2B7, Canada

  • University of Kansas Hospital

    Kansas City, Kansas, 66160, United States

  • University of Texas, MD Anderson Cancer Center

    Houston, Texas, 77030, United States

  • Universitätsklinik Mainz, Universitäts-Hautklinik, Clinical Research Center

    Mainz, 55131, Germany

  • Universitätsklinikum Schleswig-Holstein, Hämatologie/Onkologie

    Lübeck, 23538, Germany

  • Universitätsmedizin Mannheim, III. Medizinische Klinik

    Mannheim, 68167, Germany

  • Virginia Commonwealth University Medical Center

    Richmond, Virginia, 23298, United States

  • Washington University School of Medicine

    St Louis, Missouri, 63110, United States

  • Winship Cancer Institute, Emory University

    Atlanta, Georgia, 30322, United States

  • lnstituto de Estudios de Mastocitosis de Castilla la Mancha, Hospital Virgen del Valle - Complejo Hospitalario de Toledo

    Toledo, 45071, Spain

Conditions

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