Halted trial tests new injection for rare metabolic disorder
NCT ID NCT05526066
Summary
This study aimed to test the safety and drug levels of an experimental medicine called ARCT-810 in people aged 12 and older with a rare genetic condition called ornithine transcarbamylase (OTC) deficiency. Participants received either the drug or a placebo via intravenous injection up to six times. The trial was terminated early and only enrolled 8 people, so its results are very limited.
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Contacts and locations
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Locations
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Assistance Publique - Hôpitaux de Paris (AP-HP) - Hôpital Necker-Enfants Malades
Paris, France
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Azienda Ospedaliera di Padova
Padua, 35128, Italy
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Cliniques Universitaires Saint Luc
Brussels, 1200, Belgium
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Complejo Hospitalario Universitario de Santiago (CHUS) - Hospital Clínico Universitario
Santiago de Compostela, 15706, Spain
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Great Ormond Street Hospital for Children NHS Foundation Trust
London, UK, WC1N 3JH, United Kingdom
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Hospital Clínic de Barcelona
Barcelona, Spain
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Hospital Sant Joan de Déu
Barcelona, Spain
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Hospital Universitario 12 de Octubre
Madrid, 28041, Spain
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Hôpitaux Universitaires de Marseille - Hôpital de la Timone
Marseille, 13005, France
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IRCCS Ospedale Pediatrico Bambino Gesu
Rome, 00165, Italy
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Karolinska Universitetssjukhuset - Astrid Lindgrens Barnsjukhus
Stockholm, SE- 171 64, Sweden
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Salford Royal NHS Foundation Trust - Salford Royal Hospital
Salford, M6 8HD, United Kingdom
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University College London Hospitals NHS Foundation Trust - National Hospital for Neurology and Neurosurgery
London, United Kingdom
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University Hospitals Birmingham NHS Foundation Trust - Queen Elizabeth Hospital Birmingham
Birmingham, UK, B15 2PR, United Kingdom
Conditions
Explore the condition pages connected to this study.