Halted trial tests new injection for rare metabolic disorder

NCT ID NCT05526066

Summary

This study aimed to test the safety and drug levels of an experimental medicine called ARCT-810 in people aged 12 and older with a rare genetic condition called ornithine transcarbamylase (OTC) deficiency. Participants received either the drug or a placebo via intravenous injection up to six times. The trial was terminated early and only enrolled 8 people, so its results are very limited.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for ORNITHINE TRANSCARBAMYLASE DEFICIENCY are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Assistance Publique - Hôpitaux de Paris (AP-HP) - Hôpital Necker-Enfants Malades

    Paris, France

  • Azienda Ospedaliera di Padova

    Padua, 35128, Italy

  • Cliniques Universitaires Saint Luc

    Brussels, 1200, Belgium

  • Complejo Hospitalario Universitario de Santiago (CHUS) - Hospital Clínico Universitario

    Santiago de Compostela, 15706, Spain

  • Great Ormond Street Hospital for Children NHS Foundation Trust

    London, UK, WC1N 3JH, United Kingdom

  • Hospital Clínic de Barcelona

    Barcelona, Spain

  • Hospital Sant Joan de Déu

    Barcelona, Spain

  • Hospital Universitario 12 de Octubre

    Madrid, 28041, Spain

  • Hôpitaux Universitaires de Marseille - Hôpital de la Timone

    Marseille, 13005, France

  • IRCCS Ospedale Pediatrico Bambino Gesu

    Rome, 00165, Italy

  • Karolinska Universitetssjukhuset - Astrid Lindgrens Barnsjukhus

    Stockholm, SE- 171 64, Sweden

  • Salford Royal NHS Foundation Trust - Salford Royal Hospital

    Salford, M6 8HD, United Kingdom

  • University College London Hospitals NHS Foundation Trust - National Hospital for Neurology and Neurosurgery

    London, United Kingdom

  • University Hospitals Birmingham NHS Foundation Trust - Queen Elizabeth Hospital Birmingham

    Birmingham, UK, B15 2PR, United Kingdom

Conditions

Explore the condition pages connected to this study.