First human test of new Alpha-1 drug halted after early phase

NCT ID NCT02363946

Summary

This early-stage study tested a new drug called ARC-AAT to see if it was safe and could lower harmful protein levels in people with Alpha-1 Antitrypsin Deficiency, a genetic condition that can damage the lungs and liver. The trial involved 65 healthy volunteers and patients with Alpha-1, who received a single dose of either the drug or a placebo. The main goal was to check for side effects and measure how the drug behaved in the body, but the study was terminated early.

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Contacts and locations

Locations

  • Research Site 1

    Melbourne, Victoria, 3004, Australia

  • Research Site 2

    Homburg, Germany

  • Research Site 3

    Leiden, 2333ZA, Netherlands

  • Research Site 4

    Edgbaston, Birmingham, B15 2WB, United Kingdom

Conditions

Explore the condition pages connected to this study.