Early-Stage drug trial for rare lung disease halted before completion

NCT ID NCT02363946

First seen Jan 12, 2026 · Last updated May 16, 2026 · Updated 16 times

Summary

This early-phase study tested a drug called ARC-AAT in healthy volunteers and people with Alpha-1 Antitrypsin Deficiency (AATD), a genetic condition that can damage the lungs and liver. The main goal was to check safety and how the drug affects levels of a key protein. The study was terminated early, so results are limited.

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Contacts and locations

Locations

  • Research Site 1

    Melbourne, Victoria, 3004, Australia

  • Research Site 2

    Homburg, Germany

  • Research Site 3

    Leiden, 2333ZA, Netherlands

  • Research Site 4

    Edgbaston, Birmingham, B15 2WB, United Kingdom

Conditions

Explore the condition pages connected to this study.