New hope for tough blood cancers? early trial launches

NCT ID NCT06372717

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This early-stage study tests an experimental drug called APL-4098, alone or with standard treatments, in adults with acute myeloid leukemia (AML) or related blood disorders. The goal is to find a safe dose and see if it shrinks cancer. About 100 people will take part.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

APL-4098 (an experimental oral drug)

What this could lead to

If successful, this could lead to a new treatment option for people with hard-to-treat AML or MDS.

What could go wrong

This is a very early Phase 1 trial with only 100 participants, so the drug may not prove effective or safe. Side effects are unknown and could be serious.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

acute myeloid leukemia GATA2 Deficiency myelodysplastic syndrome with excess blasts

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Beatson West of Scotland Cancer Centre

    RECRUITING

    Glasgow, G120YN, United Kingdom

  • Hollywood Private Hospital

    ACTIVE_NOT_RECRUITING

    Nedlands, Western Australia, 6009, Australia

  • Monash Health

    RECRUITING

    Clayton, Victoria, 3168, Australia

  • Royal Perth Hospital

    RECRUITING

    Perth, Western Australia, 6000, Australia

  • Sarah Cannon Research Institute UK

    RECRUITING

    London, W1G 0PU, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • St. Vincent's Hospital Melbourne

    RECRUITING

    Fitzroy, Victoria, 3065, Australia

  • The Alfred Hospital

    RECRUITING

    Melbourne, Victoria, 3004, Australia

  • The Royal Marsden Hospital

    RECRUITING

    London, SM2 5PT, United Kingdom

  • University Hospital of Wales

    RECRUITING

    Cardiff, CF14 4XW, United Kingdom

    Contact