New shot method for rare lung disease shows promise in early trial
NCT ID NCT04722887
First seen Jan 04, 2026 · Last updated May 11, 2026 · Updated 23 times
Summary
This study tested a new way to give a protein replacement therapy (Alpha1-Proteinase Inhibitor) by injection under the skin instead of through a vein. It involved 17 adults with Alpha1-Antitrypsin Deficiency, a genetic condition that can damage the lungs. The main goal was to check if the treatment was safe and tolerable at two different doses given weekly for 8 weeks.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Cleveland Clinic
Cleveland, Ohio, 44195, United States
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Medical University of South Carolina - Children's Hospital
Charleston, South Carolina, 29425, United States
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UCLA Medical Center
Los Angeles, California, 90025, United States
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University of Florida
Gainesville, Florida, 32610, United States
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University of Miami
Miami, Florida, 33136, United States
Conditions
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