New pill aims to shrink painful overgrowths in rare disorder

NCT ID NCT06997588

Recruiting now Disease control Sponsor: Novartis Pharmaceuticals Source: ClinicalTrials.gov ↗

Summary

This study is testing whether a daily pill called alpelisib can safely shrink overgrowths and improve symptoms in children and adults with PROS, a rare genetic disorder that causes abnormal tissue growth. About 104 participants aged 2 and older will take the drug for up to 3 years. The main goal is to see if the treatment reduces the volume of target overgrowth lesions by at least 20%.

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Contacts and locations

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Study contacts

Contact

Phone: •••-•••-•••• Email: •••••@•••••
Contact

Phone: •••-•••-•••• Email: •••••@•••••

Locations

Novartis Investigative Site
RECRUITING

Sydney, New South Wales, 2010, Australia
Novartis Investigative Site
RECRUITING

Sydney, New South Wales, 2031, Australia
Novartis Investigative Site
RECRUITING

North Adelaide, South Australia, 5066, Australia
Novartis Investigative Site
RECRUITING

Salzburg, 5020, Austria
Novartis Investigative Site
RECRUITING

Vienna, A 1090, Austria
Novartis Investigative Site
RECRUITING

Ghent, 9000, Belgium
Novartis Investigative Site
RECRUITING

Angers, 49933, France
Novartis Investigative Site
RECRUITING

Bron, 69677, France
Novartis Investigative Site
RECRUITING

Dijon, 21000, France
Novartis Investigative Site
RECRUITING

Montpellier, 34295, France
Novartis Investigative Site
RECRUITING

Paris, 75015, France
Novartis Investigative Site
RECRUITING

Tours, 37044, France
Novartis Investigative Site
RECRUITING

Freiburg im Breisgau, Baden-Wurttemberg, 79106, Germany
Novartis Investigative Site
RECRUITING

Düsseldorf, North Rhine-Westphalia, 40225, Germany
Novartis Investigative Site
RECRUITING

Leipzig, Saxony, 04103, Germany
Novartis Investigative Site
RECRUITING

Halle, Saxony-Anhalt, 06120, Germany
Novartis Investigative Site
RECRUITING

Berlin, 13353, Germany
Novartis Investigative Site
RECRUITING

Roma, RM, 00168, Italy
Novartis Investigative Site
RECRUITING

Torino, TO, 10126, Italy
Novartis Investigative Site
RECRUITING

A Coruña, 15006, Spain
Novartis Investigative Site
RECRUITING

Madrid, 28046, Spain
Washington University
RECRUITING

St Louis, Missouri, 63110, United States

Contact

Contact Email: •••••@•••••

Conditions

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