Cancer drug shows promise for rare blood vessel disorders in kids and young adults
NCT ID NCT07543822
First seen Apr 23, 2026 · Last updated May 23, 2026 · Updated 5 times
Summary
This study tests the drug alpelisib (approved for breast cancer) in people aged 2 to 30 with certain genetic blood vessel growth disorders. Participants take the drug for at least 2 years and attend up to 16 clinic visits to check if their condition improves. The goal is to see if the drug can shrink abnormal vessels, ease symptoms, and improve quality of life.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
Conditions
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