First test of new drug for rare, debilitating disease

NCT ID NCT05661916

Summary

This study tested the safety of a new drug called ALN-TTRSC04 in healthy volunteers. The drug is designed to treat a rare disease where a harmful protein builds up in the body. Researchers gave single, increasing doses to 96 people to see how their bodies handled it and to check for side effects.

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Contacts and locations

Locations

  • Clinical Trial Site

    London, SE1 1YR, United Kingdom

Conditions

Explore the condition pages connected to this study.