New heart drug shows promise in major trial for debilitating condition
NCT ID NCT05186818
Summary
This study tested whether a new oral drug called aficamten could help adults with a specific heart condition where the heart muscle is too thick, causing symptoms like shortness of breath and limiting exercise. Over 280 participants took either the drug or a placebo pill daily for 24 weeks. The main goal was to see if the drug could safely improve how much exercise people could do and reduce their symptoms.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Aalborg University Hospital, Department of Cardiology
Aalborg, 9100, Denmark
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Alaska Heart and Vascular Institute
Anchorage, Alaska, 99508, United States
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Amsterdam UMC, location AMC
Amsterdam, 1105, Netherlands
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Ascension St. John Clinical Research Institute
Tulsa, Oklahoma, 74104, United States
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Azienda Ospedaliero Universitaria Careggi Dipartimento Cardiotoracovascolare - Cardiomiopatie Unit
Florence, 50134, Italy
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Barts Health NS Trust
London, EC1A 7BE, United Kingdom
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Beijing Anzhen Hospital
Beijing, Beijing Municipality, 100029, China
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Beijing Chao-Yang Hospital, Capital Medical University
Beijing, Beijing Municipality, 100020, China
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Brigham and Women's Hospital
Boston, Massachusetts, 02115, United States
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CHU Pitie-Salpetriere, Centre de reference maladies cardiaques hereditaires ou rares
Paris, France
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CHU de Bordeaux Hopital Cardiologique Haut-Leveque
Pessac, 33600, France
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CHU de Marseille - Hopital de la Timone Service de cardiologie
Marseille, 13005, France
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CHU de Nantes
Nantes, 44093, France
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CHU du Haut Lveque Cardiologie
Pessac, 33604, France
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Cedars-Sinai Medical Center - Smidt Heart Institute Clinic
Los Angeles, California, 90048, United States
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Centro Hospitalar Do Baixo Vouga, EPE AV ARTUR RAVARA
Aveiro, 3814-501, Portugal
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Charite-Universitaetsmedizin Berlin Campus Virchow-Klinikum (CVK) Medizinische Klinik mit Schwerpunkt Kardiologie
Berlin, 13353, Germany
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Charles University
Prague, 128 08, Czechia
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Cleveland Clinic
Cleveland, Ohio, 44195, United States
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Columbia University Medical Center/NY Presbyterian Hospital
New York, New York, 10032, United States
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Complejo Hospitalario Universitario
A Coruña, La Coruna, 15006, Spain
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Copenhagen University Hospital
Copenhagen, 2400, Denmark
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Department of Cardiology Aarhus University Hospital
Aarhus, 8200, Denmark
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Dipartimento di Medicina Clinica e Molecolare Universita Sapienza di Roma Unita di Terapia Intensiva Cardiologica Azienda Ospedaliero Universitaria Sant'Andrea
Roma, 1035-39, Italy
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Duke Health Center Arringdon
Morrisville, North Carolina, 27560, United States
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Emory Clinic
Atlanta, Georgia, 30322, United States
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Erasmus Medical Center
Rotterdam, 3015, Netherlands
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Fondazione toscana Gabriele Monesterio per la ricarca medica Dipartimento Cardiotoracico UOC Cardiologia e Medicina Cardiovasculare Ospedale San Cataldo
Pisa, 56124, Italy
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Froedtert Hospital
Milwaukee, Wisconsin, 53226, United States
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Hadassah Medical Center- Ein Kerem
Jerusalem, 9112001, Israel
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Henry Ford Medical Center
Detroit, Michigan, 48202, United States
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Hjertecentret (The Heart Center)
Copenhagen, 2100, Denmark
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Holy Cross Hospital / Cardiology Associates
Fort Lauderdale, Florida, 33308, United States
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Hopital Lariboisiere, Service de Cardiologie
Paris, 75010, France
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Hopital Universitaire de Rangueil (CHU de Toulouse) Service de Cardiologie
Toulouse, Cedex, 31059, France
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Hospital Clinic de Barcelona
Barcelona, 08036, Spain
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Hospital Clinico Universitario Virgen de la Arrixaca
Murcia, Spain
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Hospital Universitario Puerta de Hierro
Madrid, Majadahonda, Spain
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Hospital Universitario Son Llatzer Secretaria de Cardiologia
Palma, 07198, Spain
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Hospital Universitario Virgen Macarena-merge
Seville, 41009, Spain
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Hospital Universitario de Salamanca
Salamanca, 37007, Spain
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Hospital da Luz
Lisbon, 1500-650, Portugal
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Hospital of the University of Pennsylvania (University of Pennsylvania School of Medicine)
Philadelphia, Pennsylvania, 19104, United States
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Houston Methodist Hospital
Houston, Texas, 77030, United States
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Hôpital Européen Georges Pompidou
Paris, 75015, France
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Interni klinika kardiologie a angiologie
Prague, 12808, Czechia
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Kaplan Medical Center
Rehovot, 76100, Israel
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Kardio Brynow S.C
Katowice, Poland
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Kerckhoff-Klinik GmbH Abteilung Administration Forschung und Lehre
Bad Nauheim, 61231, Germany
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Klinikumder Georg-August-Universitaet
Göttingen, 37075, Germany
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Krakowskie Centrum
Krakow, Poland
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Lahey Hospital & Medical Center
Burlington, Massachusetts, 01805, United States
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Liverpool Heart and Chest Hospital - Liverpool Heart and Chest Hospital NHS Foundation Trust- HWS Greater Glasgow and Clyde
Liverpool, L14 3LB, United Kingdom
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M Health Fairview University of Minnesota Medical Center - East Bank
Minneapolis, Minnesota, 55455, United States
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Massachusetts General Hospital
Boston, Massachusetts, 02114, United States
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Mayo Clinic
Rochester, Minnesota, 55905, United States
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Mayo Clinic Florida
Jacksonville, Florida, 32224, United States
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MedStar Medical Group Cardiology at Union Memorial
Baltimore, Maryland, 21218, United States
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MedStar Washington Hospital Center
Washington D.C., District of Columbia, 20010, United States
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Medstar Franklin Square Medical Center
Baltimore, Maryland, 21237, United States
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Michigan Medicine
Ann Arbor, Michigan, 48109, United States
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Morristown Medical Center
Morristown, New Jersey, 07960, United States
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Mount Sinai Hospital
New York, New York, 10029, United States
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NYU Langone Health
New York, New York, 10016, United States
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Nanfang Hospital Southern Medical University
Guanzhou, Guangdong, 516006, China
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Narodowy Instytut Kardiologii Stefana Kardynała Wyszynskiego- Panstwowy Instytut Badawczy
Warsaw, Masovian Voivodeship, 04-628, Poland
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Northwestern University
Chicago, Illinois, 60614, United States
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Oregon Health & Science University
Portland, Oregon, 97239, United States
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Oxford Centre for Clinical Magnetic Resonance Research
Oxford, OX3 9DU, United Kingdom
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Peking University Third Hospital
Beijing, Beijing Municipality, 10019, China
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Piedmont Fayette Hospital
Fayetteville, Georgia, 30214, United States
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Queen Elizabeth Hospital Birmingham University Hospitals Birmingham NHS Foundation Trust
Edgbaston, Birmingham, B15 2GW, United Kingdom
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Queen Elizabeth University Hospital - HWS Greater Glasgow and Clyde
Glasgow, G1 4TF, United Kingdom
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Radcliffe Department of Medicine
Oxford, OX3 9DU, United Kingdom
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Royal Brompton Hospital
London, SW3 6NP, United Kingdom
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Saint Luke's Hospital of Kansas City
Kansas City, Missouri, 64111, United States
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Sanger Heart and Vascular Institute
Charlotte, North Carolina, 10595, United States
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Sanger Heart and Vascular Institute - HCM Clinic
Charlotte, North Carolina, 28204, United States
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Semmelweis Egyetem Varosmajori Sziv es Ergyogyasazati Klinika
Budapest, Hungary
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Spectrum Health Medical Group Cardiovascular Medicine
Grand Rapids, Michigan, 49525, United States
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St George's University Hospitals NHS Foundation Trust
London, SW17 0QT, United Kingdom
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Stanford University Hospital
Stanford, California, 94305, United States
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Stern Cardiovascular Foundation, Inc
Germantown, Tennessee, 38138, United States
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The Barzilai University Medical Center
Ashkelon, 78100, Israel
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The Barzilai University Medical Center
Ashkelon, 7830604, Israel
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The First Affiliated Hospital of Xi'an Jiaotong University
Xi’an, Shanxi, 710061, China
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The First Affiliated Hospital of Zhengzhou University
Zhengzhou, Henan, 450018, China
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The First Hospital of Jinlin University
Changchun, Jinlin, 130031, China
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The Ohio State University Wexner Medical Center
Columbus, Ohio, 43210, United States
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The Olga & Lev Leviev Heart Center The Chaim Sheba Medical Center
Ramat Gan, Tel Hasomer, 5265601, Israel
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The University of Texas Southwestern Medical Center
Dallas, Texas, 75390, United States
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UC San Diego Health - Sulpizio Cardiovascular Center
La Jolla, California, 92037, United States
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UOC Cardiologica Azienda Ospedaliera Spedali Civili di Brescia
Brescia, 25123, Italy
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UPMC Presbyterian
Pittsburgh, Pennsylvania, 15213, United States
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Union Hospital affiliated to Tongji Medical College of Huazhong University of Science and Technology
Wuhan, Hubei, 430022, China
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Universitaetsklinikum Essen Westdeutsches Herz-Gefaesszentrum
Essen, 45147, Germany
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Universitaetsklinikum Heidelberg
Heidelberg, Germany
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Universitaetsklinikum Jena Klinik fuer Innere Medizin 1
Jena, 07747, Germany
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Universitaetsmedizin Goettingen
Göttingen, 37075, Germany
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University Hospital Maastricht
Maastricht, 6229HX, Netherlands
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University of California San Francisco
San Francisco, California, 94143, United States
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University of Iowa
Iowa City, Iowa, 52242, United States
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University of Utah Hospital
Salt Lake City, Utah, 84132, United States
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University of Virginia Health System University Hospital
Charlottesville, Virginia, 22908, United States
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University of Washington Medical
Seattle, Washington, 98195, United States
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Universitätsklinikum Würzburg
Würzburg, Germany
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Unniversitaetsklinikum Magdeburg Klinik fur Kardiologie und Anglologie
Magdeburg, 39120, Germany
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Vanderbilt University Medical Center
Nashville, Tennessee, 37232, United States
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Washington University School of Medicine
St Louis, Missouri, 63110, United States
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Westchester Medical Center
Valhalla, New York, 10595, United States
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Xiangya Hospital of the Central South University
Changsha, Hunan, 410008, China
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Yale School of Medicine
New Haven, Connecticut, 06511, United States
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Yale University School of Medicine
New Haven, Connecticut, 06519, United States
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Ziv Medical Center
Safed, 13100, Israel
Conditions
Explore the condition pages connected to this study.