Adult PKU patients studied for brain health and life quality

NCT ID NCT01619722

First seen May 27, 2026 · Last updated Jun 13, 2026 · Updated 5 times

Summary

This study looked at 220 adults with phenylketonuria (PKU), a rare genetic condition that requires a special diet from birth. Researchers wanted to see if adults with PKU experience mental decline or other brain problems, and how the disease affects their daily life and social integration. No new treatments were tested; instead, the goal was to gather information to improve future care.

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Contacts and locations

Locations

  • APHM-Hôpital de la Conception -Médecine Interne

    Marseille, 13005, France

  • CHRU-Hôpital Bretonneau - Service de Médecine Interne-Nutrition

    Tours, Centre-Val de Loire, 37044, France

  • CHU de Dijon--Hôpital des Enfants-Centre de Génétique

    Dijon, 21079, France

  • CHU de Grenoble-Hôpital MICHALLON-Unité de Neurologie Générale

    Grenoble, 38043, France

  • CHU de LILLE-Hôpital Claude HURIEZ-Service d'Endocrinologie

    Lille, 59037, France

  • CHU de Rouen-Service de Pédiatrie

    Rouen, 76031, France

  • CHU de St Etienne-Hôpital Nord-Service de Pédiatrie

    Saint-Etienne, 42055, France

  • CHU du Morvan-Département de Pédiatrie et génétique médicale,

    Brest, 29609, France

  • CHU-ANGERS -Médecine Interne

    Angers, 49933, France

  • CHU-RENNES-Hôpital Sud-Service de Génétique-Clinique

    Rennes, 35203, France

  • CHU-Service de Réanimation Pédiatrique / Néonatalogie, Consultation spécialisée en Maladies Héréditaires du Métabolisme

    Nantes, 44000, France

  • CHU-Toulouse-Hôpital PURPAN-Service de Médecine Interne

    Toulouse, 31059, France

  • CHU_Service de Médecine Interne Nutrition A2-Hôpital du Haut Levèque

    Bordeaux, 33000, France

  • Hôpital Femme-Mère-Enfant-Centre de Référence des Maladies Héréditaires du Métabolisme de Lyon

    Bron, 69677, France

  • Hôpital Necker Enfants Malades, APHP-Maladies Métaboliques -Service de Pédiatrie

    Paris, 75743, France

  • University Hospital of NANCY

    Vandœuvre-lès-Nancy, 54500, France

Conditions

Explore the condition pages connected to this study.