New drug combo targets Hard-to-Treat brain tumors

NCT ID NCT05053880

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study investigates whether combining ACT001 (an oral drug) with pembrolizumab (an immunotherapy) can help people with recurrent glioblastoma, an aggressive brain cancer. Participants take the drugs before surgery to remove their tumor, allowing researchers to analyze how the combination affects the tumor environment. The goal is to find a safe dose and see if it improves progression-free survival.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ACT001 and pembrolizumab

What this could lead to

If it works, this combination could offer a new treatment option for recurrent glioblastoma, potentially slowing tumor progression and extending survival.

What could go wrong

This is an early-phase trial with a small number of participants, so results may not apply broadly. The drugs can cause side effects like fatigue, nausea, and immune-related reactions.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

glioblastoma neoplasm

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

More trials for these conditions

Other studies related to the condition(s) this trial covers.

Contacts and locations

Locations

  • UT MD Anderson Cancer Center, Dept of Neuro-Oncology

    Houston, Texas, 77030, United States