Tracking little lives: major study follows children with dwarfism for 5+ years

NCT ID NCT06168201

Summary

This study aims to understand how children with achondroplasia grow and develop over time, particularly those taking the medication VOXZOGO™. Researchers will follow 170 participants (mostly children under 14) for at least 5 years by collecting their medical records and asking families to complete regular questionnaires. The goal is to gather real-world information about growth patterns, health outcomes, and treatment experiences to improve future care.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Baylor College of Medicine

    RECRUITING

    Houston, Texas, 77030-2316, United States

    Contact

  • PicnicHealth

    RECRUITING

    San Francisco, California, 94107, United States

    Contact Email: •••••@•••••

  • Piedmont Health

    RECRUITING

    Statesville, North Carolina, 28625, United States

    Contact

  • Sanford Health

    RECRUITING

    Sioux Falls, South Dakota, 57105, United States

    Contact

  • UCSF

    RECRUITING

    Oakland, California, 94609, United States

    Contact

    Contact

  • University of Cincinnati

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact

  • University of Wisconsin

    RECRUITING

    Madison, Wisconsin, 53726, United States

    Contact

Conditions

Explore the condition pages connected to this study.