Gene therapy trial aims to tame rare kidney stone disease

NCT ID NCT06839235

First seen Nov 01, 2025 · Last updated May 03, 2026 · Updated 25 times

Summary

This early-stage study tests a new gene therapy called ABO-101 for people with primary hyperoxaluria type 1 (PH1), a rare genetic condition that causes painful kidney stones and kidney damage. The trial will first give a single dose to adults to find the safest amount, then test that dose in children. The main goal is to check safety and see if the treatment can lower oxalate levels in urine, which may help control the disease.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for PRIMARY HYPEROXALURIA TYPE 1 (PH1) are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Heidi Chaker

    RECRUITING

    Sfax, Tunisia

    Contact Phone: •••-•••-••••

  • Hospices Civils de Lyon- Hôpital Femmes Mères Enfants

    NOT_YET_RECRUITING

    Lyon, France

    Contact Phone: •••-•••-••••

  • Kindernierenzentrum Bonn

    NOT_YET_RECRUITING

    Bonn, Germany

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mayo Clinic

    RECRUITING

    Rochester, Minnesota, 55905, United States

    Contact Phone: •••-•••-••••

  • Nucleus Network

    WITHDRAWN

    Saint Paul, Minnesota, 55114, United States

  • Queen Elizabeth Hospital Birmingham

    RECRUITING

    Birmingham, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Royal Free Hospital

    RECRUITING

    London, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.