Unravel Biosciences, Inc.

This early-stage study is testing a drug called vorinostat to see if it is safe and might help control symptoms of Rett syndrome. Up to 15 girls and young women with Rett syndrome will take the drug at different doses, with each person also getting a placebo for comparison. The m…

This is a very early, small study to see if a drug called vorinostat is safe and might help people with Pitt Hopkins Syndrome, a rare genetic disorder. Up to 5 children and young adults will take the drug at two different doses, with periods of placebo for comparison, to check fo…