First human trial aims to lengthen telomeres, offering hope for rare genetic diseases
Disease control
Recruiting now
This early-stage trial is testing whether a combination of two oral compounds (deoxycytidine and deoxythymidine) is safe for people with rare genetic disorders called telomere biology disorders. These disorders cause very short telomeres (protective caps on chromosomes), leading …
Phase: PHASE1 • Sponsor: Suneet Agarwal • Aim: Disease control
Last updated Mar 30, 2026 14:30 UTC