New cell therapy aims to reduce chemo side effects for rare blood disease
Disease control
Recruiting now
This study tests a new way to treat Fanconi Anemia, a rare genetic disorder that causes bone marrow failure. Instead of standard high-dose chemotherapy, patients receive donor stem cells that have been specially filtered to remove certain immune cells, along with an experimental …
Phase: PHASE1, PHASE2 • Sponsor: Porteus, Matthew, MD • Aim: Disease control
Last updated May 14, 2026 12:06 UTC