Gene Therapy's lasting effects on vision tracked in Long-Term study
Disease control
Completed
This study follows people with two inherited eye conditions—choroideremia and X-linked retinitis pigmentosa—who previously received gene therapy. Researchers monitor their safety and vision over several years to see if the treatment remains safe and helps preserve sight. Particip…
Phase: PHASE3 • Sponsor: NightstaRx Ltd, a Biogen Company • Aim: Disease control
Last updated Jul 08, 2026 00:00 UTC