New drug aims to save sight in rare genetic disorder
Disease control
Not yet recruiting
This study tests whether an experimental drug called NPI-001 can slow the loss of light-sensing cells in the eyes of people with Usher syndrome, a genetic condition that causes both hearing and vision loss. About 80 adults will take either the drug or a placebo twice daily for tw…
Phase: PHASE3 • Sponsor: Nacuity Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 17, 2026 13:57 UTC