One-Shot gene therapy aims to cure devastating baby disease
⭐️ CURE ⭐️
Recruiting now
This study is testing a single-dose gene therapy called ECUR-506 in baby boys with a severe, life-threatening genetic disorder called OTC deficiency. The goal is to see if delivering a working copy of the faulty gene directly into the body is safe and can help the body properly p…
Phase: PHASE1, PHASE2 • Sponsor: iECURE, Inc. • Aim: ⭐️ CURE ⭐️
Last updated Mar 30, 2026 14:28 UTC