New study aims to unlock clues for rare childhood disease
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This study follows up to 30 children (up to age 16) with a rare genetic condition called methylmalonic acidemia (MMA). The goal is to track how the disease progresses over time by looking at blood tests and other health signs. No new treatments are tested here; instead, the infor…
Sponsor: Genespire Srl • Aim: Knowledge-focused
Last updated May 20, 2026 11:56 UTC