Gene therapy breakthrough? new trial targets Wilson's disease
Disease control
Not yet recruiting
This early-stage trial tests a one-time gene therapy called GC310 for Wilson's disease, a genetic condition that causes copper buildup. About 15 adults will receive a single IV dose and be monitored for a year to check safety and whether it improves copper levels and liver functi…
Phase: PHASE1, PHASE2 • Sponsor: GeneCradle Inc • Aim: Disease control
Last updated May 01, 2026 09:09 UTC