Real-World tracking begins for rare disease treatment
Disease control
Not yet recruiting
This study aims to collect long-term information on how well and how safely a medication called pegunigalsidase alfa works for adults with Fabry disease. It will follow about 75 patients who are already taking or planning to start this treatment in their normal healthcare setting…
Sponsor: Chiesi Italia • Aim: Disease control
Last updated Mar 23, 2026 15:15 UTC