One-Time gene therapy aims to free patients from lifelong injections
Disease control
Recruiting now
This early-stage study is testing a new, one-time gene therapy called BE-101 for adults with moderately severe or severe hemophilia B. The goal is to see if a single infusion of a patient's own genetically edited cells can safely help the body produce its own missing clotting fac…
Phase: PHASE1, PHASE2 • Sponsor: Be Biopharma • Aim: Disease control
Last updated Mar 31, 2026 12:12 UTC