X-SCID

Clinical trials for X-SCID explained in plain language.

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Scientists test 'Base Editing' to cure 'Bubble Boy' disease

⭐️ CURE ⭐️ ENROLLING_BY_INVITATION

This early-phase trial is testing a new gene therapy for X-linked Severe Combined Immunodeficiency (X-SCID), a rare and life-threatening genetic disorder that severely weakens the immune system. Researchers will collect a participant's own blood stem cells, use a precise gene-edi…

Matched conditions: X-SCID

Phase: PHASE1, PHASE2 • Sponsor: National Institute of Allergy and Infectious Diseases (NIAID) • Aim: ⭐️ CURE ⭐️

Last updated Mar 11, 2026 14:54 UTC

X-SCID

Get alerted when new X-SCID trials appear

Scientists test 'Base Editing' to cure 'Bubble Boy' disease