PROPIONIC ACIDEMIA
Clinical trials for PROPIONIC ACIDEMIA explained in plain language.
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MRNA therapy aims to tame rare metabolic disorder
Disease control Recruiting nowThis study tests an experimental mRNA medicine called mRNA-3927 for people with propionic acidemia, a rare genetic condition that causes dangerous metabolic crises. The trial involves about 77 participants, including children and infants, and aims to see if the drug is safe and c…
Matched conditions: PROPIONIC ACIDEMIA
Phase: PHASE1, PHASE2 • Sponsor: ModernaTX, Inc. • Aim: Disease control
Last updated May 15, 2026 11:53 UTC
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New mRNA therapy shows promise for rare metabolic disorder
Disease control Recruiting nowThis study looks at the long-term safety of an experimental medicine called mRNA-3927 for people with propionic acidemia, a rare genetic condition that prevents the body from breaking down certain proteins and fats. Participants have already taken part in an earlier study of this…
Matched conditions: PROPIONIC ACIDEMIA
Phase: PHASE1, PHASE2 • Sponsor: ModernaTX, Inc. • Aim: Disease control
Last updated May 13, 2026 16:04 UTC
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Researchers track rare metabolic disease to uncover its secrets
Knowledge-focused Recruiting nowThis study follows people with propionic acidemia (PA), a rare metabolic disorder, to learn how the disease affects the body over years. Participants aged 2 and older visit the clinic annually for tests like blood draws, heart checks, and brain scans. The goal is to better unders…
Matched conditions: PROPIONIC ACIDEMIA
Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Knowledge-focused
Last updated May 17, 2026 06:29 UTC
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New study aims to unlock secrets of rare metabolic disease
Knowledge-focused Recruiting nowThis study is for people with propionic acidemia, a rare genetic disorder. Researchers will look at medical records to track health events like metabolic crises and hospital visits. The goal is to better understand the disease and its impact, which may help improve future care. N…
Matched conditions: PROPIONIC ACIDEMIA
Sponsor: ModernaTX, Inc. • Aim: Knowledge-focused
Last updated May 17, 2026 06:14 UTC