NIJMEGEN BREAKAGE SYNDROME

Clinical trials for NIJMEGEN BREAKAGE SYNDROME explained in plain language.

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Not yet recruiting 1

Gentler chemo tested for rare genetic disorder to make Life-Saving transplant safer

Disease control Not yet recruiting

This study is testing a gentler chemotherapy drug called treosulfan before a stem cell transplant for patients with Nijmegen breakage syndrome, a rare genetic disorder. The goal is to see if using lower doses can reduce severe side effects and transplant-related risks while still…

Matched conditions: NIJMEGEN BREAKAGE SYNDROME

Phase: PHASE2 • Sponsor: Federal Research Institute of Pediatric Hematology, Oncology and Immunology • Aim: Disease control

Last updated Mar 30, 2026 14:34 UTC

NIJMEGEN BREAKAGE SYNDROME

Get alerted when new NIJMEGEN BREAKAGE SYNDROME trials appear

Gentler chemo tested for rare genetic disorder to make Life-Saving transplant safer