MAJOR SICKLE CELL SYNDROME OF TYPE SS OR SΒ THALASSEMIA

Clinical trials for MAJOR SICKLE CELL SYNDROME OF TYPE SS OR SΒ THALASSEMIA explained in plain language.

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Completed 1

Early step toward a gene therapy cure for sickle cell?

Disease control Completed

This small, early-stage study tested the safety and effectiveness of a single injection of a drug called plerixafor. The goal was to see if it could safely move stem cells from the bone marrow into the bloodstream of adults with severe sickle cell disease, so those cells could be…

Matched conditions: MAJOR SICKLE CELL SYNDROME OF TYPE SS OR SΒ THALASSEMIA

Phase: PHASE1, PHASE2 • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Disease control

Last updated Mar 16, 2026 15:24 UTC

MAJOR SICKLE CELL SYNDROME OF TYPE SS OR SΒ THALASSEMIA

Get alerted when new MAJOR SICKLE CELL SYNDROME OF TYPE SS OR SΒ THALASSEMIA trials appear

Early step toward a gene therapy cure for sickle cell?