LOPD

Clinical trials for LOPD explained in plain language.

Never miss a new study

Get alerted when new LOPD trials appear

Sign up with your email to follow new studies for LOPD, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Our safety recommendation!

By submitting, you agree to our Terms of use

Trials to join now! 1

One-Time gene therapy could change pompe disease treatment

Disease control Recruiting now

This study tests a single intravenous dose of a gene therapy called AB-1009 in 12 adults with late-onset Pompe disease. Participants must have been on enzyme replacement therapy for at least 6 months. The main goal is to check safety and side effects, while also seeing if the tre…

Matched conditions: LOPD

Phase: PHASE1, PHASE2 • Sponsor: AskBio Inc • Aim: Disease control

Last updated Jun 27, 2026 12:38 UTC

LOPD

Get alerted when new LOPD trials appear

One-Time gene therapy could change pompe disease treatment