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LEBERS HEREDITORY OPTIC NEUROPATHY WITH EXTRA OCULAR SYMPTOMS (LHON-PLUS)

Clinical trials for LEBERS HEREDITORY OPTIC NEUROPATHY WITH EXTRA OCULAR SYMPTOMS (LHON-PLUS) explained in plain language.

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Trials to join now! 1

First-of-its-Kind trial offers hope for devastating genetic disorders

Disease control Recruiting now

This study is testing a new oral drug called glycerol tributyrate in adults with two rare and serious genetic disorders, MELAS and LHON-Plus. The main goals are to find a safe dose for each person and to see if the drug can improve how their cells produce energy. Each participant…

Matched conditions: LEBERS HEREDITORY OPTIC NEUROPATHY WITH EXTRA OCULAR SYMPTOMS (LHON-PLUS)

Phase: PHASE1, PHASE2 • Sponsor: George Washington University • Aim: Disease control

Last updated Mar 27, 2026 12:38 UTC

LEBERS HEREDITORY OPTIC NEUROPATHY WITH EXTRA OCULAR SYMPTOMS (LHON-PLUS)

Get alerted when new LEBERS HEREDITORY OPTIC NEUROPATHY WITH EXTRA OCULAR SYMPTOMS (LHON-PLUS) trials appear

First-of-its-Kind trial offers hope for devastating genetic disorders