HEREDITARY SPASTIC PARAPLEGIA TYPE 50

Clinical trials for HEREDITARY SPASTIC PARAPLEGIA TYPE 50 explained in plain language.

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Trials to join now! 1

One-Shot gene therapy offers hope for kids with rare, devastating movement disorder

Disease control Recruiting now

This study is testing a one-time gene therapy injection for young children with a rare, inherited condition called SPG50 that severely affects movement and development. The therapy aims to deliver a working copy of the faulty gene directly to the nervous system to potentially slo…

Matched conditions: HEREDITARY SPASTIC PARAPLEGIA TYPE 50

Phase: PHASE3 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control

Last updated Mar 20, 2026 14:48 UTC

HEREDITARY SPASTIC PARAPLEGIA TYPE 50

Get alerted when new HEREDITARY SPASTIC PARAPLEGIA TYPE 50 trials appear

One-Shot gene therapy offers hope for kids with rare, devastating movement disorder