GENERALIZED ARTERIAL CALCIFICATION OF INFANCY 1

Clinical trials for GENERALIZED ARTERIAL CALCIFICATION OF INFANCY 1 explained in plain language.

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Hope for babies with Ultra-Rare fatal disease: experimental drug enters final testing phase

Disease control Recruiting now

This study is testing an investigational drug called INZ-701 in infants with a severe, ultra-rare genetic disorder called ENPP1 deficiency. The main goals are to see if the drug improves survival and prevents dangerous calcium buildup in the heart and blood vessels. About 12 infa…

Matched conditions: GENERALIZED ARTERIAL CALCIFICATION OF INFANCY 1

Phase: PHASE3 • Sponsor: Inozyme Pharma • Aim: Disease control

Last updated Mar 23, 2026 15:16 UTC

GENERALIZED ARTERIAL CALCIFICATION OF INFANCY 1

Get alerted when new GENERALIZED ARTERIAL CALCIFICATION OF INFANCY 1 trials appear

Hope for babies with Ultra-Rare fatal disease: experimental drug enters final testing phase