FAMILIAL LCAT DEFICIENCY

Clinical trials for FAMILIAL LCAT DEFICIENCY explained in plain language.

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Completed 1

One-Person trial tests hope for halting rare kidney disease

Disease control Completed

This study tested an artificial enzyme called ACP-501 in a single person with Familial LCAT Deficiency (FLD), a rare genetic disorder that causes very low 'good' cholesterol and often leads to kidney failure. Researchers wanted to see if regularly infusing this enzyme could impro…

Matched conditions: FAMILIAL LCAT DEFICIENCY

Sponsor: National Heart, Lung, and Blood Institute (NHLBI) • Aim: Disease control

Last updated Apr 02, 2026 04:11 UTC

FAMILIAL LCAT DEFICIENCY

Get alerted when new FAMILIAL LCAT DEFICIENCY trials appear

One-Person trial tests hope for halting rare kidney disease