EYE DISEASES, HEREDITARY
Clinical trials for EYE DISEASES, HEREDITARY explained in plain language.
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New eye drug aims to halt blindness in rare genetic disease
Disease control Recruiting nowThis study tests a drug called ultevursen in people with retinitis pigmentosa caused by changes in a specific part of the USH2A gene. The drug is injected into the eye and is designed to slow the loss of vision over two years. The trial includes 81 adults and children aged 8 and …
Matched conditions: EYE DISEASES, HEREDITARY
Phase: PHASE2 • Sponsor: Laboratoires Thea • Aim: Disease control
Last updated May 17, 2026 07:57 UTC
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New eye injection aims to slow rare blindness
Disease control Recruiting nowThis study tests two doses of an eye injection called VP-001 in 16 adults with a rare inherited eye disease (PRPF31 mutation) that causes vision loss. The goal is to see if repeated doses are safe and can help slow the disease. Participants must have been in a prior VP-001 study …
Matched conditions: EYE DISEASES, HEREDITARY
Phase: PHASE1, PHASE2 • Sponsor: PYC Therapeutics • Aim: Disease control
Last updated May 15, 2026 11:55 UTC
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Experimental drug aims to restore sight in rare childhood blindness
Disease control Recruiting nowThis study tests an investigational drug called sepofarsen in people with Leber congenital amaurosis (LCA), a rare genetic eye disease that causes severe vision loss from birth. The trial includes 32 participants aged 6 and older who have a specific mutation in the CEP290 gene. E…
Matched conditions: EYE DISEASES, HEREDITARY
Phase: PHASE3 • Sponsor: Laboratoires Thea • Aim: Disease control
Last updated May 13, 2026 15:59 UTC