BILE ACID SYNTHESIS DISORDERS

Clinical trials for BILE ACID SYNTHESIS DISORDERS explained in plain language.

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Can a decade of real-world data refine treatment for rare bile acid disorders?

Knowledge-focused Ongoing

This study is a patient registry that will follow people of any age with bile acid synthesis disorders who are treated with Cholbam (cholic acid). The goal is to collect information over 10 years on how the drug performs in routine clinical care, including its safety, effectivene…

Matched conditions: BILE ACID SYNTHESIS DISORDERS

Sponsor: Mirum Pharmaceuticals, Inc. • Aim: Knowledge-focused

Last updated Aug 02, 2026 00:00 UTC

BILE ACID SYNTHESIS DISORDERS

Get alerted when new BILE ACID SYNTHESIS DISORDERS trials appear

Can a decade of real-world data refine treatment for rare bile acid disorders?