BARDET-BIEDL SYNDROME 1

Clinical trials for BARDET-BIEDL SYNDROME 1 explained in plain language.

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Not yet recruiting 1

Groundbreaking eye treatment trial offers hope for rare genetic vision loss in children

Disease control Not yet recruiting

This first-in-human study aims to test the safety and find the right dose of a new treatment called AXV-101 for children aged 4-17 with Bardet-Biedl syndrome type 1 (BBS1) who have early retinal degeneration. Researchers will give a single dose to one eye and closely monitor both…

Matched conditions: BARDET-BIEDL SYNDROME 1

Phase: EARLY_PHASE1 • Sponsor: Axovia Therapeutics • Aim: Disease control

Last updated Mar 31, 2026 12:11 UTC

BARDET-BIEDL SYNDROME 1

Get alerted when new BARDET-BIEDL SYNDROME 1 trials appear

Groundbreaking eye treatment trial offers hope for rare genetic vision loss in children