AUTOSOMAL DOMINANT LEUKODYSTROPHY

Clinical trials for AUTOSOMAL DOMINANT LEUKODYSTROPHY explained in plain language.

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Not yet finished but already full! 1

Custom-Made genetic drug targets rare brain disorder in one patient

Disease control Ongoing

This study tests a personalized medicine called an antisense oligonucleotide, designed specifically for one person with autosomal dominant leukodystrophy (ADLD), a rare genetic brain disease. The treatment aims to slow or stop the disease by targeting the underlying genetic mutat…

Matched conditions: AUTOSOMAL DOMINANT LEUKODYSTROPHY

Phase: PHASE1, PHASE2 • Sponsor: n-Lorem Foundation • Aim: Disease control

Last updated Jul 15, 2026 00:00 UTC

AUTOSOMAL DOMINANT LEUKODYSTROPHY

Get alerted when new AUTOSOMAL DOMINANT LEUKODYSTROPHY trials appear

Custom-Made genetic drug targets rare brain disorder in one patient