ADENOSINE DEAMINASE DEFICIENCY

Clinical trials for ADENOSINE DEAMINASE DEFICIENCY explained in plain language.

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Not yet finished but already full! 1

Tracking gene therapy kids for 15 years: does the fix last?

Disease control ENROLLING_BY_INVITATION

This study is checking on children who were previously treated with an experimental gene therapy for a rare, severe immune system disorder called ADA-SCID. The goal is to see how safe and effective the treatment remains over 15 years by tracking their health, survival, and whethe…

Matched conditions: ADENOSINE DEAMINASE DEFICIENCY

Sponsor: University of California, Los Angeles • Aim: Disease control

Last updated Apr 01, 2026 14:40 UTC

ADENOSINE DEAMINASE DEFICIENCY

Get alerted when new ADENOSINE DEAMINASE DEFICIENCY trials appear

Tracking gene therapy kids for 15 years: does the fix last?