Diamond-Blackfan anemia
MONDO:0015253A congenital aregenerative and often macrocytic anemia with erythroblastopenia.
Also known as: Aase syndrome, Aase-Smith II syndrome, Blackfan-Diamond anaemia, Blackfan-Diamond anemia, DBA, Diamond Blackfan Anemia, Diamond-Blackfan anemia, chronic constitutional pure red cell anemia
26 clinical trials for this condition and its sub-types, 17 tagged with Diamond-Blackfan anemia itself.
Follow this condition to get notified about new trialsWhere it sits in the disease tree
Browse by category →Sub-types of Diamond-Blackfan anemia
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Diamond-Blackfan anemia 1 1 trial
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Diamond-Blackfan anemia 10 0 trials
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Diamond-Blackfan anemia 11 0 trials
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Diamond-Blackfan anemia 12 0 trials
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Diamond-Blackfan anemia 13 0 trials
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Diamond-Blackfan anemia 16 0 trials
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Diamond-Blackfan anemia 17 0 trials
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Diamond-Blackfan anemia 18 0 trials
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Diamond-Blackfan anemia 19 0 trials
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Diamond-Blackfan anemia 2 0 trials
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Diamond-Blackfan anemia 20 0 trials
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Diamond-Blackfan anemia 21 0 trials
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Diamond-Blackfan anemia 22 0 trials
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Diamond-Blackfan anemia 3 0 trials
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Diamond-Blackfan anemia 4 0 trials
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Diamond-Blackfan anemia 5 0 trials
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Diamond-Blackfan anemia 6 0 trials
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Diamond-Blackfan anemia 7 0 trials
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Diamond-Blackfan anemia 8 0 trials
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Diamond-Blackfan anemia 9 0 trials
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New hope for rare blood disorder: experimental pill reduces need for transfusions
Disease control CompletedThis study tested a drug called bitopertin in 15 adults with Diamond-Blackfan anemia (DBA), a rare inherited condition that causes severe anemia. Participants took the pill daily for 8 months, with doses possibly increasing over time. The goal was to see if the drug could raise h…
Phase 1/2 • Sponsor: National Heart, Lung, and Blood Institute (NHLBI) • Aim: Disease control
Last updated Jul 02, 2026 00:00 UTC
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New transplant cocktail aims to cut complications in bone marrow failure
Disease control CompletedThis phase 2 trial tested a combination of treosulfan, fludarabine, and rabbit antithymocyte globulin before a bone marrow transplant in 40 people with bone marrow failure diseases like Diamond-Blackfan anemia and Shwachman-Diamond syndrome. The goal was to see if this conditioni…
Phase 2 • Sponsor: Fred Hutchinson Cancer Center • Aim: Disease control
Last updated Jun 27, 2026 11:00 UTC
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One donor, two transplants: could this end lifelong Anti-Rejection drugs?
Disease control CompletedThis pilot study tested a combined bone marrow and kidney transplant from a partially matched family donor in 10 people with both a blood disorder and chronic kidney disease. The goal was to treat both conditions at once and possibly reduce the need for lifelong anti-rejection dr…
Sponsor: Massachusetts General Hospital • Aim: Disease control
Last updated Jun 27, 2026 09:10 UTC