Browse

Explore conditions, clinical trials, and the organisations running them.

← All categories

Up to: Classic organic aciduria · Hereditary anemia · Homocystinuria · Methylmalonic acidemia · Inborn disorder of cobalamin metabolism and transport

Methylmalonic aciduria and homocystinuria

An inborn error of vitamin B12 (cobalamin) metabolism characterized by megaloblastic anemia, lethargy, failure to thrive, developmental delay, intellectual deficit and seizures. There are four complementation classes of cobalamin defects (cblC, cblD, cblF and cblJ) that are responsible for methylmalonic acidemia - homocystinuria (methylmalonic acidemia - homocystinuria cblC, cblD cblF and cblJ).

1 trial tagged with this condition →